Jiang publishes research on AAV gene therapy for Tay-Sachs disease

On February 10, Xuntian Jiang, PhD and collaborators had their research titled, “AAV gene therapy for Tay-Sachs disease,” published in “Nature Medicine.”  Tay-Sachs disease (TSD) is defined as an inherited neurological disorder caused by deficiency of hexosaminidase A.   The study assesses two patients with infantile TSD in an adeno-associated virus (AAV) gene therapy expanded-access […]