In May, Xuntian Jiang, PhD and colleagues had their research titled “CRISPR-Cas9 Knock-In of T513M and G41S Mutations in the Murine β–Galactosyl-Ceramidase Gene Re-capitulates Early-Onset and Adult-Onset Forms of Krabbe Disease,” published in “Frontiers in Molecular Neuroscience.” Krabbe Disease is a genetic deficiency disorder of the lysosomal enzyme β-galactosyl-ceramidase (GALC). The correlation between reduced activity […]